Kids & teens (for parents) · Pennsylvania
Studies for children and teens in Pennsylvania
These studies only enroll people under 18. A parent or legal guardian gives permission, and children old enough to understand are asked for their own agreement (assent).
71 recruiting studiesSource: ClinicalTrials.gov, refreshed October 26, 2026How we list studies
Studies
- RecruitingPhase 4
Evaluation of SPN-812 (Viloxazine Extended-release Capsule) in Preschool-age Children With ADHD
Supernus Pharmaceuticals, Inc.
- Location
- Hershey, PA + 38 other US sites
- Eligibility basics
- Ages 4–5
- RecruitingPhase 4
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Hoffmann-La Roche
- Location
- Philadelphia, PA + 9 other US sites
- Eligibility basics
- Ages 4 mo–2
- RecruitingPhase 2
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Scholar Rock, Inc.
- Location
- Philadelphia, PA + 11 other US sites
- Eligibility basics
- Up to age 2
- RecruitingPhase 3
An Efficacy and Safety Study of Intravenous Anifrolumab to Treat Systemic Lupus Erythematosus in Pediatric Participants
AstraZeneca
- Location
- Philadelphia, PA + 18 other US sites
- Eligibility basics
- Ages 5–17
- RecruitingPhase 3
A Study of Dupilumab in Small Children With an Allergic Condition of the Esophagus (Food Pipe): Eosinophilic Esophagitis
Regeneron Pharmaceuticals
- Location
- Philadelphia, PA + 12 other US sites
- Eligibility basics
- Ages 6 mo–6
- RecruitingPhase 1
A Study to Learn About the Study Medicine Called Zavegepant (PF-07930207) in Children With a History of Migraine
Pfizer
- Location
- Philadelphia, PA + 10 other US sites
- Eligibility basics
- Ages 6–11
- RecruitingPhase 3
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
Agios Pharmaceuticals, Inc.
- Location
- Philadelphia, PA + 3 other US sites
- Eligibility basics
- Ages 1–17
- RecruitingPhase 3
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia
Agios Pharmaceuticals, Inc.
- Location
- Philadelphia, PA + 4 other US sites
- Eligibility basics
- Ages 1–17
- RecruitingPhase 2
Effect of Patiromer in Children Under 12 Years of Age With High Blood Potassium Levels
Vifor Pharma, Inc.
- Location
- Philadelphia, PA + 9 other US sites
- Eligibility basics
- Ages 0 mo–11
- RecruitingPhase 3
A Study of Guselkumab in Pediatric Participants With Moderately to Severely Active Crohn's Disease
Janssen Research & Development, LLC
- Location
- Philadelphia, PA + 8 other US sites
- Eligibility basics
- Ages 2–17
- RecruitingPhase 3
Randomized Study in Children and Adolescents With Migraine: Acute Treatment
Pfizer
- Location
- Philadelphia, PA + 69 other US sites
- Eligibility basics
- Ages 6–17
- RecruitingPhase 2
Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Crinecerfont in Participants With Classic Congenital Adrenal Hyperplasia (CAH) Who Are Less Than 4 Years Old
Neurocrine Switzerland GmbH
- Location
- Philadelphia, PA + 10 other US sites
- Eligibility basics
- Ages 4 mo–3
- RecruitingPhase 3
Study to Assess Adverse Events and Disease Activity of Oral Ubrogepant Tablets for the Acute Treatment of Migraine in Children and Adolescents (Ages 6-17)
AbbVie
- Location
- Philadelphia, PA + 87 other US sites
- Eligibility basics
- Ages 6–17
- Recruiting
Starlight Cardiovascular Lifeline Ductus Arteriosus Stent IDE Study
Starlight Cardiovascular Inc
- Location
- Philadelphia, PA + 7 other US sites
- Eligibility basics
- Up to age 6 mo
- RecruitingPhase 3
A Study to Evaluate the Efficacy, Safety, and Drug Levels of Deucravacitinib (BMS-986165) in Adolescent Participants With Moderate to Severe Plaque Psoriasis
Bristol-Myers Squibb
- Location
- Philadelphia, PA + 26 other US sites
- Eligibility basics
- Ages 12–17
- RecruitingPhase 3
Donidalorsen Treatment in Children With Hereditary Angioedema
Ionis Pharmaceuticals, Inc.
- Location
- Hershey, PA + 7 other US sites
- Eligibility basics
- Ages 2–11
- RecruitingPhase 2/Phase 3
Efficacy, Safety, and Pharmacokinetics of Vericiguat in Pediatric Participants With Heart Failure Due to Left Ventricular Systolic Dysfunction (MK-1242-036)
Merck Sharp & Dohme LLC
- Location
- Philadelphia, PA + 19 other US sites
- Eligibility basics
- Ages 1 mo–17
- RecruitingPhase 1/Phase 2
Open-label Study of SKY-GJB2 in Pediatric Subjects With GJB2-mediated Hearing Loss
Skylark Bio Inc.
- Location
- Allentown, PA + 3 other US sites
- Eligibility basics
- Ages 10 mo–7
- RecruitingPhase 3
A Study of Dulaglutide (LY2189265) 3.0 mg and 4.5 mg in Pediatric Participants With Type 2 Diabetes Mellitus (AWARD-PEDS PLUS)
Eli Lilly and Company
- Location
- Philadelphia, PA + 39 other US sites
- Eligibility basics
- Ages 10–17
- RecruitingPhase 3
Study to Evaluate Safety and Efficacy of Different PANZYGA Dose Regimens in Pediatric Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP) Patients
Octapharma
- Location
- Philadelphia, PA + 5 other US sites
- Eligibility basics
- Ages 2–17
- RecruitingPhase 2/Phase 3
A Study of Nipocalimab in Children Aged 2 to Less Than 18 Years With Generalized Myasthenia Gravis
Janssen Research & Development, LLC
- Location
- Hershey, PA + 7 other US sites
- Eligibility basics
- Ages 2–17
- RecruitingPhase 1/Phase 2
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Solid Biosciences Inc.
- Location
- Philadelphia, PA + 11 other US sites
- Eligibility basics
- Ages 0 mo–17 · Men only
- RecruitingPhase 4
Two Dose Levels of Privigen in Pediatric CIDP
CSL Behring
- Location
- Philadelphia, PA + 2 other US sites
- Eligibility basics
- Ages 2–17
- RecruitingPhase 2
Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases
Travere Therapeutics, Inc.
- Location
- Philadelphia, PA + 16 other US sites
- Eligibility basics
- Ages 1–17