Neurology · Rochester, MN
Neurology studies in Rochester, MN
19 recruiting studies have a site in Rochester.
19 recruiting studiesSource: ClinicalTrials.gov, refreshed October 26, 2026How we list studies
Studies
- RecruitingPhase 1/Phase 2
A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome
Encoded Therapeutics
- Location
- Rochester, MN + 9 other US sites
- Eligibility basics
- Ages 6 mo–17
- Recruiting
Diagnosing Epilepsy To EffeCT Change
Epiminder America, Inc.
- Location
- Rochester, MN + 21 other US sites
- Eligibility basics
- Ages 18–75
- RecruitingPhase 3
TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy
Alnylam Pharmaceuticals
- Location
- Rochester, MN + 9 other US sites
- Eligibility basics
- Ages 18–85
- RecruitingPhase 3
Randomized Study in Children and Adolescents With Migraine: Acute Treatment
Pfizer
- Location
- Rochester, MN + 69 other US sites
- Eligibility basics
- Ages 6–17
- RecruitingPhase 1/Phase 2
Treatment of Participants With Primary or Secondary Progressive Multiple Sclerosis
Tr1X, Inc.
- Location
- Rochester, MN + 7 other US sites
- Eligibility basics
- Ages 18–65
- RecruitingPhase 3
Efficacy and Safety of Intranasal Cenegermin in Adult Participants With Non-Arteritic Anterior Ischemic Optic Neuropathy (NAION)
Dompé Farmaceutici S.p.A
- Location
- Rochester, MN + 13 other US sites
- Eligibility basics
- Ages 50–80
- RecruitingPhase 1/Phase 2
ASCEND: Safety and Tolerability of ION337 for the Treatment of Dravet Syndrome
Ionis Pharmaceuticals, Inc.
- Location
- Rochester, MN + 4 other US sites
- Eligibility basics
- Ages 2–12
- RecruitingPhase 3
Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
Eidos Therapeutics, a BridgeBio company
- Location
- Rochester, MN + 39 other US sites
- Eligibility basics
- Ages 18–75
- RecruitingPhase 2
A Study of TAK-411 in Adults With Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP)
Takeda
- Location
- Rochester, MN + 11 other US sites
- Eligibility basics
- Ages 18+
- RecruitingPhase 1
AMX0114 in Adult Participants With Amyotrophic Lateral Sclerosis
Amylyx Pharmaceuticals Inc.
- Location
- Rochester, MN + 9 other US sites
- Eligibility basics
- Ages 18+
- RecruitingPhase 2
A Long-term Study of the Safety and Effectiveness of RAP-219 in Adults With Focal Onset Seizures
Rapport Therapeutics Inc.
- Location
- Rochester, MN + 6 other US sites
- Eligibility basics
- Ages 18–70
- RecruitingHealthy volunteers
ARTFL LEFFTDS Longitudinal Frontotemporal Lobar Degeneration (ALLFTD)
Mayo Clinic
- Location
- Rochester, MN + 22 other US sites
- Eligibility basics
- Ages 18+
- RecruitingHealthy volunteers
GBPDC: Gut-Brain in PD Consortium Master Protocol
Duke University
- Location
- Rochester, MN + 3 other US sites
- Eligibility basics
- Ages 21–80
- RecruitingHealthy volunteersPhase 4
Pragmatic Evaluation of Events And Benefits of Lipid-lowering in Older Adults
Duke University
- Location
- Rochester, MN + 88 other US sites
- Eligibility basics
- Ages 75+
- RecruitingHealthy volunteers
Breathing Practice for Brain and Mental Health in Cancer and Neurodegenerative Diseases
Mayo Clinic
- Location
- Rochester, MN
- Eligibility basics
- Ages 18–85
- RecruitingHealthy volunteers
Deciphering Preserved Autonomic Function After Multiple Sclerosis
Mayo Clinic
- Location
- Rochester, MN
- Eligibility basics
- Ages 18–50
- RecruitingHealthy volunteers
Late Onset Alzheimer's Disease
Columbia University
- Location
- Rochester, MN + 11 other US sites
- Eligibility basics
- Ages 55+
- RecruitingHealthy volunteers
North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
Columbia University
- Location
- Rochester, MN + 15 other US sites
- Eligibility basics
- Any age listed
- RecruitingHealthy volunteers
MR Evaluation of Cerebrospinal Fluid (CSF) Dynamics
Mayo Clinic
- Location
- Rochester, MN
- Eligibility basics
- Ages 18+
Who these studies look for
Most require a confirmed diagnosis; memory studies often ask for a study partner who knows you well to attend some visits.
Matching a page like this one never means you qualify. Each research team decides eligibility at screening.